Patients & Caregivers
Building true partnerships with patient communities is a cornerstone of our approach to every project and initiative. As the experts in the diseases we hope to treat, their input, needs, concerns, and collaboration are critical to our work.
A Patient’s Perspective
Jonathan, living with PK deficiency, and his mom, Alejandra, understand firsthand the challenges of rare diseases. Their journey highlights the importance of patient advocacy, personalized support, and access to groundbreaking therapies.
Patient Support
Agios offers the myAgios® patient support services program as a single point of engagement for eligible patients, including access support, prescription fulfillment, financial assistance, disease education and community connections. Patients and their caregivers can enroll in the program to be connected with a dedicated and clinically experienced Patient Support Manager. (U.S. residents only)
For Physicians
We recognize and appreciate the significant role that physicians play in the lives of people with rare diseases. They are a cornerstone of the community that treats and supports patients.
With medical information, grant opportunities, educational resourcesand treatment options, we aim to further their efforts on behalf of patients.
We are committed to partnering with all clinical practitioners — doctors, nurses, administration, clinical researchers — who support and treat people with rare disease.
We focus on building trusted relationships with these extended teammates, each of whom lends mission-critical insight enabling better understanding and care for patients.
We aim to further their efforts through providing educational resources, diagnostic tools, grant opportunities and research collaborations.
For more than a decade, we’ve forged new paths for gene therapies.
We custom design each of our investigational therapies with the goal of addressing the underlying cause of disease at the genetic level. We are currently developing gene therapies for severe genetic diseases and are advancing research to apply new technologies to these and other diseases. More than 170+ patients have received our therapies across 8 clinical trials.
We seek diversity, yet fly as one
We are a flock who take bold risks and collaborate with a broad community to help improve the lives of patients and families. We pride ourselves on a unique, caring, inclusive culture that helps each of us be our best every day. Honesty, respect, and a genuine commitment to access, equity and inclusivity find their way into everything we do.
Our collaboration strategy
Our mission is pursuing curative gene therapies to give patients and their families more bluebird days. We continue to develop gene therapy technologies and capabilities such as our lentiviral platform to further their application within and beyond our core indications.
We are actively seeking collaborators and licensing opportunities to explore the therapeutic potential of our technologies in new diseases.
Patient advocacy
Patient advocates and advocacy organizations are instrumental in helping us connect with and learn from the community. We are committed to building and sustaining trusting relationships and collaborations with advocates around shared goals to drive change for the communities we serve. These relationships also enable the integration of the patient and caregiver perspective throughout the nest to inform decisions made at bluebird bio.